PSC Forum 5

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The PSC Forum 5 took place on Tuesday, June 20, 2023, at ARCOTEL Wimberger Wien in Vienna, Austria

Materials

pdfAgenda

pdfParticipant List

Presentations

pdfWelcome and Introductory Remarks
Veronica Miller, Forum for Collaborative Research
Adrian Di Bisceglie, Hightide Therapeutics
Kris Kowdley, Liver Institute Northwest

Session I: Connecting The Clinic with Drug Development

pdfImplementing Recent Treatment Guidelines for PSC Clinical Trial Enrollment
Michael Trauner, Medical University of Vienna

Panel Discussion
Mary Vyas, PSC Partners Seeking a Cure Canada
Sindee Weinbaum, Hetz - Israeli Association for the Health of the Liver/European Liver Patients' Association
Martine Walmsley, PSC Support

Session II: Gaps and Barriers: Reflecting on Ongoing Programs

pdfWhat can we look at other than ALP? Innovating Biomarkers for PSC Diagnosis, Prognosis and Treatment Response
Mette Vesterhus, Norwegian PSC Research Center

pdfWhat can we look at other than ALP? Innovating Biomarkers for PSC Diagnosis, Prognosis and Treatment Response
Diana Leeming, Nordic Bioscience

pdfPanel Discussion Surrogate Endpoints for PSC: Integrating Biomarkers into Clinical Trials
Michelle Berrey, Intercept Pharmaceuticals
Lisa Boyette, Gilead Sciences, Inc.
Matthew Frankel, Chemomab Therapeutics
Eric Lefebvre, Pliant Therapeutics
Leigh MacConell, Ipsen
Charles McWherter, CymaBay Therapeutics, Inc.
Benjamin Miller, Ipsen
Tiago Nunes, Mirum Pharmaceuticals
Tim Watkins, Gilead Sciences, Inc.

Session III: Collaborations Across Datasets

pdfOverview
Veronica Miller, Forum for Collaborative Research

Session IV: Next Steps

Comments
Adrian Di Bisceglie, HighTide Therapeutics
Kris Kowdley, Liver Institute Northwest
Veronica Miller, Forum for Collaborative Research


* Indicates remote participation