Pediatric Cholestatic Disease Working Group Introductory CallFriday, March 19, 2021 MaterialsPresentationsJessica Weber, Forum for Collaborative Research Stakeholder Perspectives On Demonstrating Efficacy And Safety In Clinical Trials:Saul Karpen, Emory University School of Medicine/ Children’s Healthcare of Atlanta Henkjan Verkade, University of Groningen Roberta Smith, Alagille Syndrome Alliance Pediatric Drug Development: FDA Perspective Ruby Mehta, U.S. Food and Drug Administration Overview of Current Paediatric Investigation Plans: EMA Perspective Chrissi Pallidis, European Medicines Agency Pam Vig, Mirum Pharma
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